We are dedicated to improving the lives of people affected by muscular dystrophy and related neuromuscular conditions

What we do

Muscular dystrophy and related neuromuscular conditions are regarded as rare and, in many cases, even ultra-rare conditions. There are currently no efficient treatments or cures available for most of these conditions. Research, however, advances fast and a number of clinical trials to test the clinical benefit of promising technology are under way.

Over more than 50 years, the charity has contributed to crucial scientific breakthroughs in the field of muscular dystrophy and related neuromuscular conditions such as: laying the foundations for the promising technology of 'exon skipping' which is currently being tested in clinical trials for boys with Duchenne muscular dystrophy, and funding work that has led to a scientific breakthrough in finding a treatment for mitochondrial myopathy, which is now close to clinical trial.

Scientists and clinicians are beginning to express cautious optimism that treatments might become a reality in the near future, but to do this we need to continue to fund research. We aim to find treatments and ultimately cures for muscular dystrophy and related neuromuscular conditions and improve the lives of everyone affected by them and we need your help to do this.

Our work has five main focuses:

We rely almost entirely on voluntary donations and legacies to fund our work. Dedicated volunteers,companiestrusts and foundations help us to raise money to fund our vital work.