Pompe Disease
There are 11 clinical trials
-
A registry of patients with Pompe disease
Location: North America
Status: Recruiting -
A study of the safety and effectiveness of immune suppressing drugs prior to treatment with Myozyme for infantile-onset Pompe disease
Location: North America
Status: Ongoing but has finished recruiting patients -
A study to test whether it is safe and beneficial to induce the immune system to become tolerant of Myozyme in patients with Pompe disease
Location: Middle East, North America
Status: Recruiting -
Alglucosidase alfa temporary access programme
Location: North America
Status: Approved For Marketing -
Documenting the progression of late-onset Pompe disease symptoms
Location: Asia
Status: Recruiting -
Improving the efficacy of enzyme replacement therapy for Pompe disease
Location: Europe, North America, United Kingdom
Status: Recruiting -
Phase 1 trial of BMN 701 in patients with late-onset Pompe disease
Location: North America
Status: Recruiting -
Registry of breastfeeding women with Pompe disease treated with Myozyme
Location: North America
Status: Recruiting -
Registry of pregnant women with Pompe disease treated with Myozyme
Location: North America
Status: Recruiting -
Safety study of gene therapy for Pompe Disease
Location: North America
Status: Recruiting
