Spinal Muscular Atrophy
There are 11 clinical trials
-
A study testing olesoxime as a treatment for spinal muscular atrophy type 2 and 3
Location: Europe, United Kingdom
Status: Ongoing but has finished recruiting patients -
A study testing valproic acid and carnitine in infants with spinal muscular atrophy type 1
Location: Europe, North America
Status: Ongoing but has finished recruiting patients -
A trial of hydroxyurea in spinal muscular atrophy
Location: Asia
Status: Completed -
Genetic testing for spinal muscular atrophy patients and carriers
Location: Asia
Status: Completed -
International SMA patient registry.
Location: North America
Status: Recruiting -
Pilot study of growth hormone to treat spinal muscular atrophy type II and III
Location: Europe
Status: Ongoing but has finished recruiting patients -
Sodium phenylbutyrate in pre-symptomatic infants with spinal muscular atrophy
Location: North America
Status: Recruiting -
Study of a cough assist device for individuals with neuromuscular conditions
Location: Europe
Status: Terminated -
Testing the safety of strength training in spinal muscular atrophy
Location: North America
Status: Recruiting -
Testing the safety, tolerability and dosing of an antisense drug approach (ISIS-SMNRx) in children with spinal muscular atrophy
Location: North America
Status: Recruiting



