Research news
Duchenne muscular dystrophy:
- 1 May 2013
Sarepta Therapeutics update Over the past few weeks Sarepta Therapeutics have announced updates about their clinical trials and pre-clinical research into exon skipping technology. - 12 April 2013
GSK announces results of exon skipping trial At a conference in the USA, Glaxosmithkline has announced preliminary results from a phase 2 clinical trial of exon skipping technology in boys with Duchenne muscular dystrophy. - 27 March 2013
Behind the scenes laboratory visit for families Families affected by Duchenne muscular dystrophy saw firsthand the progress Professor George Dickson and his team are making in pioneering work into treatments for Duchenne muscular dystrophy, as they toured their laboratories. - 8 March 2013
Side effects reported in GSK exon skipping trials GSK has announced that several participants in exon skipping clinical trials have experienced side effects. However, we remain confident that the safety of boys in the trials is a priority and that all boys are being carefully monitored. - 19 February 2013
Duchenne muscular dystrophy steroid trial launched Researchers led by Professor Katie Bushby in Newcastle have launched a clinical trial that aims to identify the best way for doctors to give corticosteroids to boys with Duchenne muscular dystrophy - 8 February 2013
Study of long-term steroid use in boys with Duchenne muscular dystrophy A group of researchers led by Prof. Francesco Muntoni has published the results of a study into long-term steroid use in boys with Duchenne muscular dystrophy. - 31 January 2013
Prosensa awarded orphan drug status Prosensa has received orphan drug status for further molecular patches both in Europe and the USA. - 1 January 2013
Ataluren update from PTC Therapeutics PTC therapeutics has recently given an update on the development of ataluren. - 27 November 2012
Professor Francesco Muntoni awarded EU Health Innovation Grant A team of scientists led by Prof Francesco Muntoni has been awarded an EU Health Innovation grant to develop a molecular patch for exon 53 of the dystrophin gene. - 22 November 2012
New drug to be tested for use in the muscular dystrophies Researchers at the Royal Veterinary College, University of London have received a grant from the Medical Research Council to investigate an experimental drug for its ability to delay the progression of muscular dystrophy.
