Pompe disease

There is presently research into a treatment for Pompe in progress and there are clinical trials.

Contents:

• To read about present research developments, please visit this website: www.genzyme.com/pompe/pompe_clinical.asp



• Treatment is not presently available except for infantile-onset Pompe patients and for severely ill late onset patients. There is soon likely to be a clinical treatment programme in the UK for Pompe. To find out more, click this link: www.genzyme.com/pompe/pompe_home.asp.